Are We About to Cure Sickle-Cell Disease?

March 22, 2022

(The New Yorker) – Many scientists, including Frangoul, caution that it’s too early to say definitively that gene therapy is a cure. (We don’t know what will happen down the road; patients in the CRISPR trial will be followed for fifteen years.) Still, the early signs are encouraging.Vertex Pharmaceuticals and CRISPR Therapeutics, the companies that developed the technique, announced last year that all seven of the sickle-cell patients in their trial had experienced a resolution of their sickle-cell crises. (Read More)