Angiodema: Gene Therapy Blocks Painful Hereditary Disorder

February 1, 2024

3D rendering of a DNA molecule

(BBC) – Gene therapy has transformed the lives of people with a genetic disorder that causes painful and unpredictable swelling attacks. Angiodema, thought to affect 50,000 people worldwide, can be seriously debilitating, affect airways, and occasionally prove fatal. Patients treated with a single dose of gene therapy Crispr-Cas9 showed little sign of further symptoms. (Read More)