Pioneering Gene Therapy Restores UK Girl’s Hearing

May 9, 2024

3D rendering of a DNA molecule

(BBC) – A UK girl born deaf can now hear unaided, after a groundbreaking gene-therapy treatment. Opal Sandy was treated shortly before her first birthday – and six months on, can hear sounds as soft as a whisper and is starting to talk, saying words such as “Mama”, “Dada” and “uh-oh”. Given as an infusion into the ear, the therapy replaces faulty DNA causing her type of inherited deafness. Opal is part of a trial recruiting patients in the UK, US and Spain. (Read More)