17 and Going Blind: The High Stakes of Getting into a Gene Therapy Trial

September 20, 2016

(MIT Technology Review) – The problem is that the traditional system for clinical trials isn’t equal to the urgency patients like Gary face. To get into a clinical trial for gene therapy, patients must meet specific criteria set by drug makers. Among other things, the patients must fall into a certain age group and must have had symptoms for a defined period of time. Gary was fortunate enough to petition for the rules of one trial to be changed so he could enter. But many other people aren’t so lucky.