Hemophilia Trial Finds Promising Cure
December 18, 2017
(CNN) – A gene-therapy trial by London researchers has seen remarkable success in finding a long-term cure for hemophilia A. The trial, by researchers at Barts Health NHS (National Health Service) Trust and Queen Mary University of London, used gene therapy to inject one dose of a missing gene in patients with the condition, and the gene continued functioning in the body for more than a year. This is the first successful gene therapy to treat the condition.