Tests Suggest Scientists Have Achieved First ‘in Body’ Gene Editing in Bid to Treat Rare Disease

February 11, 2019

(The Japan Times) – Scientists think they have achieved the first gene editing inside the body, altering DNA in adults to try to treat a disease, although it is too soon to know if this will help. Preliminary results suggest that two men with a rare disorder now have a corrective gene at very low levels, which may not be enough to make the therapy a success. Still, it’s a scientific milestone toward one day doctoring DNA to treat many diseases caused by faulty genes.

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