Blind Patients Hope Landmark Gene-Editing Experiment Will Restore Their Vision

May 10, 2021

(NPR) – Kalberer and Knight are two of the first patients treated in a landmark study designed to try to restore vision to patients such as them, who suffer from a rare genetic disease. The study involves the revolutionary gene-editing technique called CRISPR, which allows scientists to make precise changes in DNA. Doctors think CRISPR could help patients fighting many diseases. It’s already showing promise for blood disorders such as sickle cell disease and is being tested for several forms of cancer. But in those experiments, doctors take cells out of the body, edit them in the lab and then infuse the genetically edited cells back into patients.