Girl, Eight, with Rare Brain Disorder in Pioneering UCL Stem Cell Research
February 24, 2017
(MSN) – A girl of eight whose rare brain disorder is likely to lead to her death when she is in her teens is taking part in pioneering stem cell research in a bid to save others with same condition. Lily Harriss’s skin cells will first be turned into stem cells and then into brain cells by researchers at University College London as they seek treatments or a cure. About 100 to 200 cases of BPAN — beta-propeller protein-associated neurodegeneration — are known worldwide, although this is believed to be an underestimate.